This December 1993 microscope photo provided by the National Cancer Institute shows a typical neuroblastoma with rosette formation. (Dr. Maria Tsokos/National Cancer Institute via AP) From Philly and ...

The experimental therapy focuses on hereditary deafness and one rare condition only. Genes are responsible for as much as 60% of deafness and hearing loss in children. Gene therapy has allowed several ...

Dr. Katherine High is CEO of RhyGaze. From the Philadelphia Business Journal: Almost five years after leaving Spark Therapeutics, Dr. Katherine High is back at the helm of a gene therapy company with ...

To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Preview this article 1 min The new CEO had a key role in ...

An 11-year-old boy is able to hear for the very first time in his life thanks to a groundbreaking gene therapy procedure, according to the Children's Hospital of Philadelphia (CHOP). The boy -- who ...

You may have noticed a giant steel structure rising at 30th and Chestnut streets over the last few months — the site that will eventually be Spark Therapeutics’ new Gene Therapy Innovation Center, and ...

PHILADELPHIA (WPVI) -- The Children's Hospital of Philadelphia says it's used gene therapy for the first time in the U.S. to treat genetic hearing loss. An 11-year-old boy received the experimental ...

(AP) — Dr. Alfonso Sabater pulled up two photos of Antonio Vento Carvajal's eyes. One showed cloudy scars covering both eyeballs. The other, taken after months of gene therapy given through eyedrops, ...

After spending over 300 days at the Children's Hospital of Philadelphia (CHOP), 9-month-old KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene editing therapy.

Philadelphia needs to remind investors the city can do it all in life sciences and reestablish its bona fides as a fitting headquarters location for leading companies. That was the word from panelists ...

A new gene therapy developed at the Children's Hospital of Philadelphia has been approved by the FDA and is being used to transform lives. The first patient to receive this gene therapy after it was ...

Gene therapy has allowed several children born with inherited deafness to hear. A small study published Wednesday documents significantly restored hearing in five of six kids treated in China. On ...